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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Human Umbilical Vein Endothelial Cells
Multi resolution modeling
Long QT
CaVβs
Cell Line
Cell homeostasis
Invivo
Multi exon skipping
DMO
Immunoglobulin Fc Fragments/pharmacology
Muscle Biology
MiARN
Muscular Dystrophy
Humans
Calcium
DHPR α1S
Muscle
Mice
Genomic
Becker muscular dystrophy BMD
Becker muscular dystrophy
Dystrophie Musculaire de Becker BMD
Dystrophie Musculaire de Duchenne DMD
Dystrophin
LncARN
Mitochondrial fission
Skeletal muscle
Cell Biology
Hepatocellular carcinoma
Activin Receptors
Allele‐specific silencing therapy
Multiresolution modeling
Becker BMD muscular dystrophy
Centronuclear myopathy
Muscle development
NAD+
Autophagy
Myotendinous junction
Muscle Strength
Duchenne muscular dystrophy
LncRNA
Hear
Exon skipping
Gene modifiers
Cells
Energy Metabolism/drug effects
Gene expression
Liver
MES
Morphogenesis
Animal/physiopathology
NNOS
Cardiomyopathy
CaV subunits
Modificateurs de gènes
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Génomique
Muscular Atrophy
Antisense oligonucleotides
Cultured
DMD
Base Sequence
Homeostasis
Calcium Channels
Diseases
Cachexia
Epigenetics
Dystrophine
Molecular docking
Drp1
Gene Expression Regulation/drug effects
Muscles/physiopathology
Ex-vivo
CTNNB1
Male
Muscular dystrophy
Metabolism
Molecular Sequence Data
CD38
Delivery
Myogenesis
Inbred C57BL
Knockout
Clinical trials
Mdx mouse
Animals
BMD
Cardiomyopathie
Long noncoding RNA
Dystrophie musculaire de Becker
Inhibitors
Dystrophin central domain
Dystrophy
Dystrophin-EGFP
Duchenne DMD dystrophy
Inbred mdx
L-Type
Duchenne muscular dystrophy DMD
LKB1
Dynamin 2